Our Programs

Our Programs

Our Approach

Focus on treatments for people living with serious and rare diseases

Akcea is focused on addressing the unmet needs and complex medical challenges of patients with important, but less understood, serious and rare disorders.

Hereditary transthyretin (hATTR) amyloidosis

Learn more about hATTR amyloidosis – a rare, genetic disease.

Familial chylomicronemia syndrome (FCS)

Learn more about FCS – a rare, metabolic disorder.